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BioMarin Pharmaceutical

NASDAQ · BMRN·San Rafael, CA·Large-cap·Approved

Commercial-stage rare disease biopharma with seven approved products including VOXZOGO (vosoritide) for achondroplasia, ROCTAVIAN (gene therapy for hemophilia A), PALYNZIQ for PKU, and several enzyme replacement therapies. Pipeline includes BMN 333 and BMN 351.

Decks (1)

TitleOccasionDateSlidesSource
BioMarin Q4 2025 Earnings PresentationEarningsFebruary 26, 202622PDF