Alnylam Pharmaceuticals Inc.
NASDAQ · ALNY·Cambridge, MA·Large-cap·Approved
RNAi therapeutics pioneer with six approved siRNA medicines (Amvuttra/Onpattro for ATTR amyloidosis, Givlaari, Oxlumo, Qfitlia, and partnered Leqvio for hypercholesterolemia) and a deep clinical pipeline spanning cardiometabolic, CNS, and rare disease. Following Amvuttra's HELIOS-B win in ATTR-CM, the company unveiled its "Alnylam 2030" strategy targeting 25%+ revenue CAGR and TTR market leadership.
Decks (1)
| Title | Occasion | Date | Slides | Source |
|---|---|---|---|---|
| Alnylam 2026 J.P. Morgan Presentation | JPM Healthcare | January 12, 2026 | 27 |